Alexander Disease, and the First Drug Approved to Treat It
Astrocytes immunostained for glial fibrillary acidic protein (GFAP) — the protein whose overproduction causes Alexander disease. Yann Bernardinelli, 2013, CC BY-SA 3.0, via…
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The First Approved Treatment for Ataxia in Ataxia-Telangiectasia
The cerebellum (bottom right) — the part of the brain that degenerates in ataxia-telangiectasia. Henry Vandyke Carter, from Gray's Anatomy, 20th ed. (1918), plate 720, public…
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